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Pompe Disease Treatment Market Size

  • Report ID: GMI8315
  • Published Date: Feb 2024
  • Report Format: PDF

Pompe Disease Treatment Market Size

Pompe Disease Treatment Market size was valued at USD 1.6 billion in 2023 and is expected to grow at a CAGR of 4.4% between 2024 and 2032. Pompe disease, also known as glycogen storage disease type II, is a rare genetic disorder caused by mutations in the GAA gene. It results in deficient activity of the enzyme GAA, leading to the accumulation of glycogen in cells, particularly in muscles, causing progressive weakness and other symptoms.

 

The market growth is due to the escalated burden of Pompe disease, leading to increased demand for effective treatments. This trend has fueled research activities, including the development of innovative therapeutic approaches like enzyme replacement therapy (ERT) and ongoing studies on alternative therapies. Pompe disease results from acid alpha-glucosidase (GAA) deficiency, with incidence rates varying by ethnicity and region. The highest prevalence occurred in East Asian populations (1 in 12,125). The growing global burden has driven the need for enhanced diagnosis and care access for the patients with rare diseases treatment, thereby bolstering the market growth.

 

Authors: Mariam Faizullabhoy, Gauri Wani

Frequently Asked Questions (FAQ) :

The market size of pompe disease treatment reached USD 1.6 billion in 2023 and is set to cross USD 2.3 billion by 2032, due to the escalated burden of Pompe disease, leading to increased demand for effective treatments.

Monotherapy segment is expected to record a CAGR of 4.4% over 2024 and 2032, due to its simplicity and effectiveness in managing Pompe disease.

North America market accounted for a revenue share of 37.8% in 2023, driven by the proliferation of novel drug launches, a robust presence of pharmaceutical companies in the region, and increased R&D investments.

Abeona Therapeutics Inc., Amicus Therapeutics, Inc., Aro Biotherapeutics Company, Audentes Therapeutics (Astellas Pharma Inc.), Bayer AG, F. Hoffmann-La Roche Ltd., Genethon, Maze Therapeutics, M6P Therapeutics, Oxyrane, Sanofiare some of the major industry contenders.

Pompe Disease Treatment Market Scope

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Premium Report Details

  • Base Year: 2023
  • Companies covered: 12
  • Tables & Figures: 249
  • Countries covered: 19
  • Pages: 170
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